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Spinraza Access and Sites

We will continue to update our community on administration sites, insurance coverage, and community resources and support programs for Spinraza.

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Conference Conference Conference

2018 Annual SMA Conference

Registration is now open for the 2018 Annual SMA Conference, scheduled for June 14 -17, 2018 at the Hilton Anatole Hotel in Dallas, TX!

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Events Events Events

Spring Events

Spring event season is on its way. Join us! Find an upcoming event in your area, or host your own event.

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2018 Updated SMA Drug Pipeline Released

2018 Updated SMA Drug Pipeline Released

We’ve recently released an update to the SMA drug pipeline. This latest version includes:

AveXis Announces Expanded Clinical Development Program for AVXS-101 in Spinal Muscular Atrophy

AveXis Announces Expanded Clinical Development Program for AVXS-101 in Spinal Muscular Atrophy

AveXis, a clinical-stage gene therapy company developing treatments for patients suffering from rare and life-threatening neurological genetic...

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Scholar Rock Announces Plan to Bring Possible SMA Treatment into Clinical Trials

Scholar Rock Announces Plan to Bring Possible SMA Treatment into Clinical Trials

Scholar Rock, a biotechnology company based in Boston, has announced that they will be investing nearly $50 million to bring SRK-105, a muscle...

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Cure SMA Launches Advocacy Action Network

Cure SMA Launches Advocacy Action Network

Working together, we’ve achieved tremendous success in advocating for ourselves, our families, and our whole community, particularly in...

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Minnesota Becomes Second State to Adopt Newborn Screening for SMA

On December 27, the Minnesota Commissioner of Health accepted the recommendation of the state's Advisory Committee on Heritable and Congenital...

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