We’ve recently released an update to the SMA drug pipeline. This latest version includes: 23 active programs, including two approved therapies. 15 pharmaceutical partners. 6 programs in clinical trials. An ever-increasing breadth of potential treatment approaches to SMA. Effective Treatments for All Ages, Stages and Types of SMA The updated version of this pipeline reflects […]
Updated SMA Drug Pipeline Now Available Read More »
Cytokinetics, Incorporated, today announced that data from two preclinical studies of reldesemtiv were presented at the 2019 Annual Cure SMA Conference in Anaheim, CA, showing that the addition of reldesemtiv to treatment with SMN upregulators (nusinersen and SMN-C1, an analogue to risdiplam) significantly increased muscle force in a mouse model of spinal muscular atrophy (SMA).
The 2019 Annual SMA Conference, now in its 31st year, is set to kick off on June 28 and continue into a weekend full of programs and events that bring families, researchers and healthcare professionals together. This year’s conference will be the largest to date. We’re expecting a record number of 2,500 attendees, including over
The 2019 Annual SMA Conference is Here! Read More »
Cure SMA is pleased to announce receipt of $150,000 grant over three years, awarded by the Oscar G. and Elsa S. Mayer Family Foundation to support continued development of the SMA Care Center Network. The mission of the SMA Care Center Network is to: Improve SMA clinical care and disease management, leading to creation of
Cure SMA Receives $150,000 Grant From the Oscar G and Elsa S Mayer Family Foundation Read More »
Laura Watson is team captain of Laura’s Dream Team and fundraising committee co-chair of the North New Jersey Cure SMA Chapter. On Saturday, June 22, 2019, Laura is joining over 150 people at the 4th Annual North Jersey Walk-n-Roll. My name is Laura Watson. I am 29 years old and was born and raised (and
Community Spotlight: Laura Watson Read More »
The 2019 Annual SMA Conference booklet is now available for download. The booklet includes information on workshops, special events and details of the Annual SMA Conference, including: 1. A complete schedule, full agenda, and descriptions and speaker bios for the 55 workshops. 2. Details about many of the special events planned during the Annual SMA
The 2019 Annual SMA Conference Booklet is Now Posted Online Read More »
The Family Friendly Research Poster Session will be held on Saturday, June 29th from 6:30pm to 8:00pm at the 2019 Annual SMA Conference. The Family Friendly Research Poster Session allows for one-on-one interactions between families and researchers. Cure SMA has invited researchers, who are attending SMA Researcher Meeting, to present family friendly research posters. During
Family Friendly Research Poster Session Presenters Announced Read More »
Dear members of the SMA community, We are grateful for the opportunity to continue to help support individuals with spinal muscular atrophy (SMA), their caregivers and families. We deeply appreciate our shared goals and are dedicated to helping people with SMA, of all ages, and welcome the addition of new treatments in order to provide
Biogen Issues Q2 Community Statement on Spinraza Read More »
Happy Global Running Day! Is Global Running Day a made-up holiday? Kind of. But unlike other made-up holidays dedicated to eating pancakes or taking selfies, Global Running Day has the purpose of celebrating running and encouraging people to get active. Today, we’d love for you to celebrate Global Running Day by joining or supporting Team
Team Cure SMA Celebrates Global Running Day! Read More »
Scholar Rock today announced positive final top-line results from the Phase 1 clinical trial of its product candidate, SRK-015, a highly specific inhibitor of myostatin activation, in healthy adult volunteers. Consistent with previously announced interim findings, the final results showed robust and sustained target engagement and no apparent safety signals were observed across all tested
