At the end of June, SMA researchers and clinicians from around the world met in Orlando, Florida, for the 2023 Annual SMA Research & Clinical Care Meeting. The annual meeting provides an opportunity for SMA scientists and clinicians to share their most recent discoveries and learnings, and is an incubator for collaborations, including cross-disciplinary […]
Genentech recently issued an SMA community statement highlighting updates from the 2023 SMA Research & Clinical Care Meeting. These updates included: Investigating risdiplam treatment post gene-therapy Long-term efficacy and safety of risdiplam Real-world evidence generation Check out the full community statement here.
Genentech Releases SMA Community Letter Read More »
On July 27th, the U.S. Senate Appropriations Committee supported a Cure SMA-requested provision asking the National Institutes of Health (NIH) to address the unmet needs of individuals with spinal muscular atrophy (SMA) through new SMA research. The provision, which can be found on pages 132 & 133 of the fiscal year 2024 Labor-Health and Human
Key Congressional Committee Urges NIH to Address Unmet Needs of Individuals with SMA Read More »
Whether you have SMA, have a loved one with SMA, are a researcher, care provider, industry partner, or are new to the SMA community, SMA Awareness Month is a time to come together to celebrate, honor, reflect, remember, and learn. The theme of SMA Awareness Month 2023 is ‘Breakthroughs Begin with You.’ It’s an opportunity
August is SMA Awareness Month! Read More »
