Author name: Morgan Tuttle

Meet the National Disability Employment Awareness Month (NDEAM) Panelists

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October is National Disability Employment Awareness Month (NDEAM)! Hear directly from adults living with SMA in the workforce. Register for Cure SMA’s first NDEAM webinar. The 60-minute webinar will be held on Wednesday, October 24 at 2:00 p.m. CDT. Register today! Kaitlyn Yang @KaitlynYang At age nine, Kaitlyn Yang emigrated to the U.S. from China […]

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National Disability Employment Awareness Month Spotlight: Kim Hill

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The below NDEAM Spotlight was written by Kim Hill, Disability Integration Specialist at the Oklahoma Department of Emergency Management, who also lives with SMA Type II.  Hello! My name is Kimberly or Kim Hill. I am a 34-year-old from Oklahoma with SMA Type II. I am trached and use a ventilator full time and I

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Register for Cure SMA’s First National Disability Employment Awareness Month Webinar

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October is National Disability Employment Awareness Month (NDEAM)! In its honor, Cure SMA is hosting our first NDEAM webinar where the audience will hear directly from adults living with SMA in the workforce. Register for Cure SMA’s first NDEAM webinar today.  The 60-minute webinar will be held on Wednesday, October 24 at 2:00 p.m. CDT. NDEAM

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AveXis Issues Community Statement on FDA Filing for SMA Type I

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AveXis has provided the following community statement on their FDA filing for SMA type I. Dear SMA Community, AveXis, a Novartis company, is pleased to let you know that we have submitted regulatory applications for AVXS-101 in the U.S., Europe and Japan for use in infants with SMA Type 1. This is an important and

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AveXis Files for FDA Approval of Gene Therapy for Spinal Muscular Atrophy
Type I

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AveXis, Inc., a Novartis company, today announced that they have filed for FDA approval of AVXS-101, a gene therapy that replaces the survival motor neuron 1 (SMN1) gene, which is missing or mutated in individuals with SMA. This first filing is for intravenous (IV) delivery of gene therapy. Based on typical practices, the expectation is

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Type I Read More »

North Carolina to Screen Newborns for SMA Through Early Check

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Early Check, a new research study led by RTI International, is now available for newborn babies in North Carolina. Early Check is a free screening study designed to identify children with rare health conditions before symptoms appear and study the benefits of early treatments. New and expectant mothers may enroll in the program online from

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Breakthrough Prize Awarded to Adrian Krainer and Frank Bennett for SMA Research Leading to Spinraza

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Collaborators Adrian Krainer, of Cold Spring Harbor Laboratory, and C. Frank Bennett, from Ionis Pharmaceuticals, received the 2019 Breakthrough Prize in Life Sciences. They won for the development of the first effective therapy for spinal muscular atrophy, Spinraza. Dr. Krainer is a long time member of the the CURE SMA Scientific Advisory Board, and his

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Cure SMA Receives Generous Funding from Luke 18:1 Foundation

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Cure SMA would like to thank the Luke 18:1 Foundation for their generous donations to our equipment pool and research programs. The foundation’s generosity will provide support and hope to all those affected by SMA. The Luke 18:1 Foundation was started by Nicole and Daniel Stickane in honor of their son Luke who was diagnosed

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SMA Care Center Network and Clinical Data Registry Launched

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Cure SMA today announced the launch of our SMA Care Center Network. The SMA Care Center Network is the centerpiece of our efforts to address the changing landscape of SMA. The goal of the SMA Care Center Network is to develop an evidence-based standard of care that will improve the lives of all those affected

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