Author name: Sarah McCall

Cure SMA Launches “Spotlight on SMA” Partnership with Neurology Reviews

Cure SMA is pleased to announce the release of “Spotlight on SMA: The Urgent Need for Early Diagnosis in Spinal Muscular Atrophy,” a supplement developed in collaboration with Neurology Reviews. The goal of this partnership is to enhance current awareness and understanding of SMA diagnostic requirements, while emphasizing the importance of early treatment as it […]

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Lights…Camera…Action! Search Is On for Child with SMA to Appear in NBC Television Pilot

Cure SMA is excited to support casting directors from NBC as they search for boys and girls from the SMA community who are interested in playing a character with spinal muscular atrophy in an upcoming 20th Century Fox pilot. The team is currently focusing their search on children aged 7-11 years of age in the Chicagoland

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Cure SMA Adds New Equipment Item for Teens and Adults with SMA

Along with funding SMA research and offering clinical care services, Cure SMA provides thousands of affected individuals and families with vital support and resources that help them navigate daily life with SMA. We are thrilled to add to our equipment pool inventory the Panthera S3 Swing—a lightweight manual wheelchair for adults and teens living with

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Genentech’s Risdiplam Meets Primary Endpoint in Pivotal FIREFISH Trial in Infants with Type 1 SMA

Genentech, a member of the Roche Group, today announced positive topline results from the pivotal Part 2 of the FIREFISH study, evaluating risdiplam in infants aged 1-7 months with Type 1 spinal muscular atrophy (SMA). The primary outcome measure of the study was the proportion of infants sitting without support for at least five seconds

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Annual SMA Conference Registration Continues to Grow!

The 2020 Annual SMA Conference registration numbers are growing quickly! We expect the 2020 conference – which includes both the Family Conference and the Research & Clinical Care Meeting – will be one of our biggest ever. Hotel rooms in our block are filling up, so be sure to register and make your hotel reservations

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Cure SMA and Biogen to Co-Host Webinar on DEVOTE Clinical Trial – Register Today!

On Tuesday, February 4th, at 11am CST (9am PST/10am MST/12pm EST) Biogen and Cure SMA will co-host a webinar for the SMA community. During the webinar, you’ll hear from Biogen about the latest information on its SPINRAZA clinical trial, DEVOTE, a Phase 2/3 randomized, controlled dose-escalating study with infantile and later-onset SMA of all ages,

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A Look Back at 2019: Cure SMA Research Year-in-Review

During our last fiscal year—July 1, 2018, to June 30, 2019—Cure SMA funded more than $7 million in new research and ongoing research. The resources will help accelerate research and ensure we are developing treatments for all types, ages, and stages of SMA. The areas funded include: Basic research, with a focus on funding approaches

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Cure SMA Awards Grants to Four States to Expediate the Implementation of SMA Newborn Screening

With an incidence of approximately one in 11,000, more than 360 infants will be born annually with spinal muscular atrophy (SMA). Newborn screening can help to pre-empt irreversible motor neuron loss, increase prompt intervention, and eliminate long diagnostic delays. The impact of early diagnosis has been demonstrated through several studies that reinforce the importance of

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