Clinical Trial Readiness
SMA Industry Collaboration
The Cure SMA Clinical Trial Readiness Program is an initiative developed under the SMA Industry Collaboration. Our goal is to alleviate challenges related to site capacity and enhance patient access to SMA clinical trials. The program offers resources for clinical research sites that seek to evaluate and optimize their readiness for SMA trials. Materials were created with input from the SMA patient community, health care providers, clinical researchers, and trial sponsors to highlight the evolving needs of SMA patients and families in an ever-changing landscape.
Readiness Checklists
Cure SMA has created companion checklists to help clinical research professionals examine their preparedness for SMA clinical trials. Two checklists are available: one for trial sites and a second for clinical evaluators.
These were created with input from established research sites and sponsors of SMA clinical trials. For copies, please email [email protected].
Toolkits on SMA, Clinical Evaluation, and Clinical Research Coordination
Cure SMA has created a trio of toolkits for research teams. We have also compiled a list of resources from other organizations that may be helpful. We welcome feedback and ideas for topics to address. To receive information about future events and share your ideas, please email us at [email protected].
Cure SMA has compiled information on numerous external resources from reputable sources that will be helpful to new and experienced research teams and, in particular, PTs and CRCs. These include training checklists, reading material, and information about online and in-person courses and workshops.
DOWNLOAD RESOURCES ON SMA, GENETIC DISEASES, AND CLINICAL RESEARCH TOPICS
Workshops and Webinars
In conjunction with its Annual SMA Conference, Cure SMA periodically hosts workshops for clinical research coordinators (CRCs), physical therapists (PTs), and clinical evaluators (CEs). To attend, individuals must register for the Research & Clinical Care Meeting.
Cure SMA also organizes webinars, which are recorded and available via Cure SMA’s Clinical Trial Readiness Program YouTube playlist.
SMArt Moves as a Resource
Developmental delays can be early signs of a serious medical condition. If something about a child’s development doesn’t feel quite right, don’t delay. SMArt Moves educates parents and healthcare providers about the signs of delayed milestones. With SMA, early diagnosis and treatment are key. Check out SMArt Moves!
