Front Page News
Community Statement from AveXis Regarding Commitment to SMA Community Amid COVID-19 Pandemic
Dear SMA Community, Like many organizations across the United States and around the world, AveXis is closely monitoring the coronavirus […]
Read More ›Community Statement from Genentech on Risdiplam Approval Timeline
Dear SMA Community, As part of our ongoing partnership and following your request to receive important information about the risdiplam clinical […]
Read More ›Answering Your Coronavirus (COVID-19) Medical Questions
We want you to know that Cure SMA continues to be here for the entire SMA community. We remain vigilant in monitoring and responding to […]
Read More ›Biogen Announces First Patient Treated With Higher Dose Of Spinraza In Phase 2/3 DEVOTE Study
Biogen today announced that the first patient has been treated in the global clinical study, DEVOTE. The study is designed to evaluate the safety, tolerability, […]
Read More ›Zolgensma® Data Shows Rapid, Significant, Clinically Meaningful Benefit in SMA, Including Prolonged Event-free Survival, Motor Milestone Achievement and Durability, Now Up to 5 Years Post-dosing
AveXis, a Novartis company, announced a one-time infusion of Zolgensma® (onasemnogene abeparvovec-xioi) showed rapid, significant, and clinically meaningful therapeutic benefit in patients with spinal muscular […]
Read More ›Cure SMA Launches Part 2 of “Spotlight on SMA” in Partnership with Neurology Reviews
Cure SMA is pleased to announce the release of “Spotlight on SMA: The Spinal Muscular Atrophy Treatment Landscape,” the final supplement in a two-part series […]
Read More ›Cure SMA Announces Additional Event Cancellations; No Changes to Plans and Recommendations for Annual SMA Conference
As news about the Coronavirus (COVID-19) continues to evolve, Cure SMA has now decided to cancel all events (i.e., galas, dinners, Walk-n-Rolls, Summits of Strength) […]
Read More ›2020 Annual SMA Conference Schedule is Released
Cure SMA has released the schedule for the 2020 Annual SMA Conference, which will be held at Disney’s Yacht & Beach Club Resorts in Orlando, Fla., […]
Read More ›Grant Announcement: Cure SMA Awards $150,000 Grant to Emily Welby, Ph.D., Medical College of Wisconsin
This article is part of a series of Cure SMA grant announcements being shared throughout the winter/spring. Cure SMA has awarded a $150,000 grant to […]
Read More ›Biogen Issues Community Letter with Perspective on Coronavirus (COVID-19)
Dear SMA Community, We want to provide an update on Biogen’s efforts to help ensure the health and safety of the SMA community amid the […]
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