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Cure SMA Working Group Revises Recommendations for the Treatment of Infants Diagnosed with SMA via Newborn Screening Who Have 4 Copies of SMN2

February 14, 2020
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To help clinicians and the families they serve in the decision of when to administer therapy to infants identified with SMA via newborn screening, Cure […]

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Cure SMA Launches “Spotlight on SMA” Partnership with Neurology Reviews

February 11, 2020
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Cure SMA is pleased to announce the release of “Spotlight on SMA: The Urgent Need for Early Diagnosis in Spinal Muscular Atrophy,” a supplement developed […]

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Celebrate Rare Disease Day 2020 with Cure SMA

February 7, 2020
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This year, Rare Disease Day occurs on February 29—the rarest day of all! Spinal muscular atrophy (SMA) affects 12,000 people in the U.S. Yet, the […]

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Lights…Camera…Action! Search Is On for Child with SMA to Appear in NBC Television Pilot

February 6, 2020
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Cure SMA is excited to support casting directors from NBC as they search for boys and girls from the SMA community who are interested in […]

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Genentech’s Risdiplam Showed Significant Improvement in Motor Function in People Aged 2-25 Years with Type 2 or Type 3 SMA

February 6, 2020
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Genentech, a member of the Roche Group, today presented 1-year data from the pivotal Part 2 of the SUNFISH study, evaluating risdiplam in people aged […]

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Cure SMA Adds New Equipment Item for Teens and Adults with SMA

January 28, 2020
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Along with funding SMA research and offering clinical care services, Cure SMA provides thousands of affected individuals and families with vital support and resources that […]

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Summit of Strength Program Dates Confirmed

January 27, 2020
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Cure SMA is happy to announce the schedule for the 2020 Summit of Strength Program! Currently entering its third year, we have brought together nearly […]

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Genentech’s Risdiplam Meets Primary Endpoint in Pivotal FIREFISH Trial in Infants with Type 1 SMA

January 23, 2020
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Genentech, a member of the Roche Group, today announced positive topline results from the pivotal Part 2 of the FIREFISH study, evaluating risdiplam in infants […]

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Annual SMA Conference Registration Continues to Grow!

January 10, 2020
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The 2020 Annual SMA Conference registration numbers are growing quickly! We expect the 2020 conference – which includes both the Family Conference and the Research […]

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Community Statement from Scholar Rock Regarding SRK-015

January 10, 2020
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Scholar Rock, a clinical-stage biopharmaceutical company focused on the treatment of serious diseases in which protein growth factors play a fundamental role, today highlighted key […]

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