Front Page News
Cure SMA Working Group Revises Recommendations for the Treatment of Infants Diagnosed with SMA via Newborn Screening Who Have 4 Copies of SMN2
To help clinicians and the families they serve in the decision of when to administer therapy to infants identified with SMA via newborn screening, Cure […]
Read More ›Cure SMA Launches “Spotlight on SMA” Partnership with Neurology Reviews
Cure SMA is pleased to announce the release of “Spotlight on SMA: The Urgent Need for Early Diagnosis in Spinal Muscular Atrophy,” a supplement developed […]
Read More ›Celebrate Rare Disease Day 2020 with Cure SMA
This year, Rare Disease Day occurs on February 29—the rarest day of all! Spinal muscular atrophy (SMA) affects 12,000 people in the U.S. Yet, the […]
Read More ›Lights…Camera…Action! Search Is On for Child with SMA to Appear in NBC Television Pilot
Cure SMA is excited to support casting directors from NBC as they search for boys and girls from the SMA community who are interested in […]
Read More ›Genentech’s Risdiplam Showed Significant Improvement in Motor Function in People Aged 2-25 Years with Type 2 or Type 3 SMA
Genentech, a member of the Roche Group, today presented 1-year data from the pivotal Part 2 of the SUNFISH study, evaluating risdiplam in people aged […]
Read More ›Cure SMA Adds New Equipment Item for Teens and Adults with SMA
Along with funding SMA research and offering clinical care services, Cure SMA provides thousands of affected individuals and families with vital support and resources that […]
Read More ›Summit of Strength Program Dates Confirmed
Cure SMA is happy to announce the schedule for the 2020 Summit of Strength Program! Currently entering its third year, we have brought together nearly […]
Read More ›Genentech’s Risdiplam Meets Primary Endpoint in Pivotal FIREFISH Trial in Infants with Type 1 SMA
Genentech, a member of the Roche Group, today announced positive topline results from the pivotal Part 2 of the FIREFISH study, evaluating risdiplam in infants […]
Read More ›Annual SMA Conference Registration Continues to Grow!
The 2020 Annual SMA Conference registration numbers are growing quickly! We expect the 2020 conference – which includes both the Family Conference and the Research […]
Read More ›Community Statement from Scholar Rock Regarding SRK-015
Scholar Rock, a clinical-stage biopharmaceutical company focused on the treatment of serious diseases in which protein growth factors play a fundamental role, today highlighted key […]
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