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Cure SMA Update on Data Accuracy Issues with AveXis’ SMA Therapy, Zolgensma

August 9, 2019
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Earlier this week, the FDA issued a statement identifying data accuracy issues with AveXis’ SMA therapy, Zolgensma. Cure SMA immediately opened an investigation into the […]

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Cure SMA Releases Status Update on Data Accuracy Issues with Zolgensma

August 7, 2019
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Yesterday, the FDA issued a statement identifying data accuracy issues with Avexis’ SMA therapy, Zolgensma. Cure SMA is in communication with the FDA and is committed to […]

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FDA Issues Statement on Data Accuracy Issues with Recently Approved Gene Therapy

August 6, 2019
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Today, the FDA issued the below statement identifying data accuracy issues with AveXis’ SMA therapy, Zolgensma. Cure SMA is investigating this issue and will report when we have […]

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Biogen Issues Community Statement on Spinraza

August 5, 2019
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Biogen has provided the following community statement on Spinraza. Dear members of the SMA community, Following a busy spring of data presentations at medical congresses […]

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SMA Awareness Month 2019 Has Begun!

August 1, 2019
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SMA Awareness Month occurs in August! The SMA community officially recognizes August as Spinal Muscular Atrophy Awareness Month and Cure SMA has been coordinating activities […]

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Biogen Announces New NURTURE Data at the 2019 Annual SMA Conference

July 1, 2019
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Biogen today announced new results from the NURTURE study, adding data to the longest study of spinal muscular atrophy (SMA) in pre-symptomatic infants (n=25). These […]

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Updated SMA Drug Pipeline Now Available

June 28, 2019
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We’ve recently released an update to the SMA drug pipeline. This latest version includes: 23 active programs, including two approved therapies. 15 pharmaceutical partners. 6 […]

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Cytokinetics Releases New Data from Reldesemtiv Clinical Study at the 2019 Annual SMA Conference

June 28, 2019
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Cytokinetics, Incorporated, today announced that data from two preclinical studies of reldesemtiv were presented at the 2019 Annual Cure SMA Conference in Anaheim, CA, showing […]

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The 2019 Annual SMA Conference is Here!

June 26, 2019
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The 2019 Annual SMA Conference, now in its 31st year, is set to kick off on June 28 and continue into a weekend full of […]

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Cure SMA Receives $150,000 Grant From the Oscar G and Elsa S Mayer Family Foundation

June 25, 2019
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Cure SMA is pleased to announce receipt of $150,000 grant over three years, awarded by the Oscar G. and Elsa S. Mayer Family Foundation to […]

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