Front Page News
Scholar Rock Announces Positive Interim Results from Phase 1 Trial of SRK-015 in Healthy Volunteers and Updates on Future Development Plans
Scholar Rock today announced positive interim results from the ongoing Phase 1 single- and multiple-ascending dose clinical trial of SRK-015 in healthy adult volunteers. SRK-015, […]
Read More ›Community Spotlight: Kristen Smith
The SMA community has been lobbying state and federal government for years. Kristen Smith shares how she became involved with advocacy. Kristen Smith describes herself […]
Read More ›Arkansas and Florida Adopt SMA Newborn Screening
We are thrilled to share that both Arkansas and Florida recently adopted SMA to their state newborn screening panels! They now join the growing list […]
Read More ›Cure SMA Awards $150,000 Grant to Veronica Pessino, PhD, Salk Institute for Biological Sciences
Audrey Lewis founded Families of SMA, now Cure SMA, 34 years ago. Audrey recognized early on the importance of attracting new and talented researchers to […]
Read More ›Community Spotlight: Amber Bosselman
Amber Bosselman is your typical 22-year-old college senior. She is currently studying psychology in Idaho and planning to get her master’s degree in industrial psychology. […]
Read More ›Show Your Rare. Show You Care.
1 in 20 people will live with a rare disease at some point in their life. Rare Disease Day improves knowledge amongst the general public […]
Read More ›Cure SMA Awards $150,000 Grant to Laxman Gangwani, PhD, Texas Tech University
Cure SMA has awarded a $150,000 research grant to Laxman Gangwani, PhD, at the Texas Tech University Health Sciences Center, for his project entitled, “Function […]
Read More ›Register for Cure SMA’s Advocacy 101 Webinar: Learn How to Make a Difference
On Wednesday, February 20th at 12pm CST (10am PST/11am MST/1pm EST) Cure SMA’s Policy and Advocacy team will hold a webinar to update the SMA […]
Read More ›The Cure SMA 2019 Goal List
Start 2019 strong! Plan out your year using the Cure SMA 2019 Goal List. Have you completed any of the items already? Which ones will […]
Read More ›Cure SMA’s 2019 Commitments to the Community
Dear Friends, Welcome to 2019! The start of the new year is a fantastic opportunity for us to share the exciting things we have planned […]
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