Front Page News
Clinical Research and Drug Development Session Highlights from 2024 Annual SMA Research & Clinical Care Meeting
During the first week of June, SMA researchers and clinicians from around the world met in Austin, Texas, for the 28th Annual SMA Research & […]
Read More ›Spring 2024 Issue of Compass Now Available
The Spring 2024 issue of Compass is now available online. This year, we are proud to announce six new research grants, totaling $750,000, to […]
Read More ›Thank You for an Amazing 2024 Annual SMA Conference!
Thank you to everyone who attended the 2024 Annual SMA Conference at the JW Marriott in Austin, Texas! It was an impactful weekend of opportunities […]
Read More ›SMA Researchers and Clinicians from Around the World Gather at the 28th Annual SMA Research & Clinical Care Meeting
During the first week of June, SMA researchers and clinicians from around the world met in Austin, Texas, for the 28th Annual SMA Research & […]
Read More ›Cure SMA Announces Additional $750,000 in Basic Research Funding
At the Annual SMA Research and Clinical Care Meeting, Cure SMA highlighted six new basic research grants totalling $750,000. Cure SMA also announced another $750,000 […]
Read More ›Five-Year Data for Genentech’s Evrysdi Show the Majority of Treated Children With a Severe Form of SMA Achieved or Maintained the Ability to Sit, Stand or Walk
Summary of Data Presented After 5 years of treatment, 91% of children were alive – without treatment, children with Type 1 SMA would not be […]
Read More ›Spinal Muscular Atrophy (SMA) Update in Best Practices: Recommendations for Diagnosis Considerations
Cure SMA is pleased to announce the publication of the first in a series of new resources to support the care of individuals living with […]
Read More ›Novartis Gene Therapies Releases Spring SMA Community Letter
Novartis Gene Therapies recently released an update to the SMA community related to clinical trials and long term follow up studies of Zolgensma, in addition […]
Read More ›Cure SMA Attends Spring 2024 Professional Organization Conferences to Promote Findings from Industry Collaboration Initiatives
Cure SMA is pleased to announce the participation of scientific leadership in the 2024 Muscular Dystrophy Association (MDA) Virtual Clinical & Scientific Conference (March 3 […]
Read More ›SMA Community Advocacy Results in Key Accessible Air Travel Win
On May 16, after more than 2-years of advocacy and education by the SMA and disability communities, Cure SMA-supported legislation was signed into law making […]
Read More ›