Front Page News
Novartis Announces FDA Filing Acceptance and Priority Review for AVXS-101
Novartis today announced that the U.S. Food and Drug Administration (FDA) has accepted the company’s Biologics License Application (BLA) for AVXS-101, now known as ZOLGENSMA® […]
Read More ›Register for Cure SMA’s Webinar on SMA Treatments and Clinical Trials
On Wednesday, December 12th, at 12:00pm CST (10:00am PST/11:00am MST/1:00pm EST) Cure SMA will hold a webinar updating the community on the latest information on […]
Read More ›Scholar Rock Announces Publication of Preclinical Data on the Therapeutic Benefit of Inhibiting Myostatin Activation in Models of SMA
Scholar Rock, a clinical-stage biopharmaceutical company focused on the treatment of serious diseases in which protein growth factors play a fundamental role, today announced the […]
Read More ›Cure SMA Launches “SMArt Moves” for Early Diagnosis and Treatment
Cure SMA today launches SMArt Moves, a new disease awareness and educational campaign to empower parents, pediatricians and other healthcare professionals to swiftly recognize and […]
Read More ›8th Annual “Hope on the Hill” Congressional Dinner Will Be Held Later This Month in Washington D.C.
The 8th Annual “Hope on the Hill” Congressional Dinner will be held on Tuesday, November 27, bringing together SMA families, government officials, and industry leaders […]
Read More ›Cure SMA is Thrilled to Launch a New Support Program for Teens and Adults with SMA
Along with funding SMA research and care, Cure SMA provides thousands of individuals and families with vital family support and resources that help people navigate […]
Read More ›Summit of Strength Program Receives Positive Feedback and Increases Attendance
Attendance and feedback have been extremely positive for this new program. The Cure SMA Summit of Strength Program kicked off in July and has continued […]
Read More ›Registration is Now Open for the 2019 Annual SMA Conference!
Registration is now open for the 2019 Annual SMA Conference! This year’s conference will be held at the Disneyland Hotel in Anaheim, CA from Friday, […]
Read More ›Kansas Adopts SMA Newborn Screening as Several Other States Move Closer to Adoption
Progress is currently being made in several states for getting SMA added to Newborn Screening panels. We are delighted to share this news with you […]
Read More ›Meet the NDEAM Webinar Panelists
October is National Disability Employment Awareness Month (NDEAM)! Hear directly from adults living with SMA in the workforce. Register for Cure SMA’s first NDEAM webinar. […]
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