Front Page News
Congratulations to the Winners of Cure SMA’s Video Contest!
Cure SMA recently hosted a video contest to raise SMA awareness and provide the opportunity for teens and young adults (aged 12 to 21) to […]
Community Spotlight: Rebecca Smith and Micah Biello
When Micah Biello was diagnosed with spinal muscular atrophy type 1, no one in his family knew about the disease. Now four years later, Micah’s […]
Genentech, Roche and PTC Therapeutics Provide Update on Regulatory Filing for Risdiplam
On January 7th, PTC Therapeutics, Inc. provided a corporate update, which will be detailed as part of the company’s presentation at the 37th Annual J.P. […]
Teen and Young Adult Survey Extended Through January 21st
Are you or a family member between the ages of 12 and 25? Do you want to share your opinion on living with SMA and […]
Community Spotlight: The Jankowski Family
It has been a little over two years since doctors told Chris and Kelly Jankowski that their first-born son, William, had spinal muscular atrophy (SMA) […]
Cure SMA Announces Expanded Phase 3 of SMA Industry Collaboration
Cure SMA is pleased to announce the launch of an expanded Phase 3 of our SMA Industry Collaboration. The SMA Industry Collaboration is a multi-faceted […]
Hope on the Hill Congressional Dinner Raises $200,000
The 8th Annual “Hope on the Hill” Congressional Dinner was held on Tuesday, November 27, 2018 at The Willard Hotel in Washington, DC. More than […]
December Webinar on SMA Treatments and Clinical Trials Now Available Online
A recording of the December 13th webinar updating the community on SMA treatments and clinical trials is now available online. A PDF of the webinar […]
2018 Research Year-in-Review
Over our past fiscal year—from July 1, 2017, to June 30, 2018—Cure SMA has funded over $5 million in new research funding. This funding will be […]
Cure SMA Funding Leads to 16 New Research Publications in 2018
An important goal of our research funding strategy is to share scientific findings with the broader scientific community. Scientists who receive Cure SMA funding often […]