Front Page News
SMA Community Leaders to Gather in Washington DC to Network, Learn and Advocate
On Thursday, April 26, more than 70 chapter leaders, event organizers and board/committee members, representing 24 states and DC, will gather in Washington DC for […]
Read More ›The Discovery of Spinraza
SMA is caused by a mutation in the survival motor neuron gene 1 (SMN1). In a healthy person, this gene produces a protein—called survival motor […]
Read More ›There is Still Time to Complete Cure SMA’s 2018 Community Survey
Dear Members of the SMA Community, For the past several years, we’ve been working to collect data and information on our community’s experiences, goals, hopes, […]
Read More ›Biogen Presents New Data at the American Academy of Neurology (AAN) Annual Meeting
Biogen recently presented new data on Spinraza for the treatment of spinal muscular atrophy (SMA) during the 70th American Academy of Neurology (AAN) Annual Meeting, […]
Read More ›Spring 2018 Issue of Compass Now Available Online
The Spring 2018 issue of Compass is now available online. The issue covers Cure SMA’s newborn screening efforts, including how NBS can help children diagnosed […]
Read More ›Registration for the 2018 Annual SMA Conference Closes in Two Weeks
The deadline to register for the 2018 Annual SMA Conference is just two weeks away! Registration will close on Friday, May 4th. Over 1,100 people […]
Read More ›Genentech to Present New RG7916 Data at the American Academy of Neurology (AAN) Annual Meeting
Genentech/Roche announced today that new data on its approved and investigational medicines for neurological conditions will be presented during the 70th American Academy of Neurology […]
Read More ›Cure SMA Awards $150,000 Grant to Bakri Elsheikh, MD, Ohio State University Wexner Medical Center
Cure SMA has awarded a $150,000 research grant to Bakri Elsheikh, MD, at the Ohio State University Wexner Medical Center, for his project, “Determine the […]
Read More ›Cure SMA Database Findings Published in the Journal of Neuromuscular Diseases
An important goal at Cure SMA is to collect data to better understand the SMA patient population, and then to report this data back to […]
Read More ›Novartis Agrees to Acquire AveXis
AveXis, Inc. and Novartis announced today that they have entered into an agreement and plan of merger. Novartis will acquire AveXis in a transaction unanimously […]
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