Front Page News
House and Senate Vote to Increase Federal Funding for Newborn Screening Programs
Today, Congress passed a new federal spending bill, increasing funding for several critical newborn screening programs, that the President also signed. The bill increases funding for the […]
Read More ›Cure SMA Awards $150,000 Grant to Charlotte Sumner, MD, Johns Hopkins University
Cure SMA has awarded a $150,000 research grant to Charlotte Sumner, MD, at Johns Hopkins University, for her project, “Testing the potential of SMN-AS1 as […]
Read More ›Record Number of Abstracts Submitted for 2018 SMA Researcher Meeting
Abstract submission is now closed for the 2018 SMA Researcher Meeting. We are excited to announce that we received 128 submissions, a record number. Our […]
Read More ›The Discovery of SMA
In 2016, the spinal muscular atrophy community celebrated the approval of the first-ever treatment that targets the underlying genetic cause of SMA. This was a […]
Read More ›Roche Releases Community Statement on RG7916 and Olesoxime Programs
Roche has provided the following community statement on RG7916 and Olesoxime investigational programs. Dear SMA Community, We are very pleased to share an update of […]
Read More ›Cure SMA Awards $75,000 Grant to Robert Kalb, MD, Northwestern University
Cure SMA has awarded a $75,000 research grant to Robert Kalb, MD, at Northwestern University Feinberg School of Medicine, for his project, “Effects of diminished […]
Read More ›Cure SMA to Host Inaugural Clinical Care Meeting
Clinicians across the country are invited to share experiences, successes and ideas at the inaugural SMA Clinical Care Meeting to be held on Saturday, June 16, […]
Read More ›Cure SMA Awards $150,000 Grant to Umrao Monani, PhD, Columbia University
Cure SMA has awarded a $150,000 research grant to Umrao Monani, PhD, at Columbia University, for his project, “SMA modulators as a means to revealing […]
Read More ›Biogen Announces New Interim Phase 2 Results From NURTURE
Biogen recently announced new interim Phase 2 results from NURTURE, the ongoing open-label, single-arm study evaluating the efficacy and safety of SPINRAZA or nusinersen among […]
Read More ›Cure SMA Launches Second Annual Community Survey to Address Important Issues in SMA Treatment
Dear Members of the SMA Community, For the past several years, we’ve been working to collect data and information on our community’s experiences, goals, hopes, […]
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