Front Page News
Applications for Cure SMA Medical Advisory Council Due October 15th
Cure SMA is expanding its role in spinal muscular atrophy medical affairs at the national level through its Medical Advisory Council (MAC). The MAC sets […]
Read More ›Genentech/Roche Releases Clinical Trial Update for RG7916
Genentech/Roche recently provided the following community statement with clinical trial updates for SUNFISH (Type 2/3). The SUNFISH trial is advancing to part two, which is […]
Read More ›2017 SMA Awareness Month Recap
The SMA community celebrated an impactful and advocacy-driven Awareness Month through a number of ways this August. Whether hosting candlelight vigils, meeting with state and […]
Read More ›Cure SMA to Host Webinar Updating the Community on Spinraza Access
On Tuesday, September 19, at 12:00pm CST (10:00am PST/11:00am MST/1:00pm EST), Cure SMA will hold a webinar updating the community on the status of Spinraza […]
Read More ›2017 SMA Researcher Meeting Summary: Clinical Research Studies for SMA
The Annual SMA Researcher Meeting is the largest research meeting in the world specifically focused on SMA. This year we had a record setting 470 […]
Read More ›2017 Researcher Meeting Summary: Identification of Candidate Therapeutic Targets and Disease Modifiers
The Annual SMA Researcher Meeting is the largest research meeting in the world specifically focused on SMA. This year we had a record setting 470 […]
Read More ›Victor Dubowitz Honored at 2017 Researcher Meeting for Early Contributions to the SMA Field
During the 2017 SMA Researcher Meeting, we honored one of our 2017 conference champions, Dr. Victor Dubowitz. Dr. Dubowitz’s early contributions to the SMA field […]
Read More ›SMA Documentary Premieres at 2017 Rhode Island International Film Festival
Life & Atrophy, a film about SMA, premiered at the Rhode Island International Film Festival on Saturday, August 12th. It was directed, produced, edited and […]
Read More ›Cure SMA-Funded Researchers, Diane Murrell and Deborah Boroughs, Publish Papers
Two Cure SMA-funded projects have recently been published. Diane Murrell and her team published the paper, “The Experience of Families With Children With Spinal Muscular […]
Read More ›2017 Researcher Meeting Summary: Regulation of Splicing and SMN Protein Expression
The Annual SMA Researcher Meeting is the largest research meeting in the world specifically focused on SMA. This year we had a record setting 470 […]
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