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Cure SMA Receives Generous Donations from Fighting for Kaiden Foundation

April 4, 2017
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Cure SMA would like to thank the Fighting for Kaiden Foundation for their generous donations to our equipment pool and research programs. The foundation’s generosity […]

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Record Number of Abstracts Submitted for the 2017 SMA Researcher Meeting

March 29, 2017
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Abstract submission is now closed for the 2017 SMA Researcher Meeting. We are excited to announce that we received 125 submissions, a record number. Our […]

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Cytokinetics Announces Start of Second Cohort in Phase 2 Clinical Trial of CK-2127107 in Patients with SMA

March 29, 2017
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Cytokinetics, Inc. today announced that the second cohort of the Phase 2 clinical trial of CK-2127107 in patients with spinal muscular atrophy (SMA), is open […]

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Cure SMA Coverage and Payment Policy Project Continues to Move Forward

March 23, 2017
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The Cure SMA Coverage and Payment Policy Project has two distinct but complementary tracks: Outreach on behalf of our community. We’re working with public and […]

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Genentech Roche Releases Community Letter with Clinical Trial Updates

March 21, 2017
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Genentech Roche provided the following community statement with clinical trial updates for SUNFISH (Type 2/3), FIREFISH (Type 1) and JEWELFISH. Dear SMA community, At Genentech […]

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Cure SMA Releases Schedule for the 2017 Annual SMA Conference

March 21, 2017
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Cure SMA has released the schedule for the 2017 Annual SMA Conference, to be held at Walt Disney World in Orlando, FL, June 29 – […]

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Cure SMA Awards $140,000 Grant to Joceyln C̫t̩, PhD, University of Ottawa

March 21, 2017
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Cure SMA has awarded a $140,000 research grant to Joceyln Côté, PhD, at The University of Ottawa, for his project, “Investigating the mechanism by which […]

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American College of Obstetricians and Gynecologists Recommends Expanded SMA Carrier Screening

March 20, 2017
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The American College of Obstetricians and Gynecologists has released updated guidance on carrier testing for genetic conditions. The updated guidance includes, for the first time, […]

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AveXis Reports Results from Phase 1 Trial of AVXS-101

March 16, 2017
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AveXis, Inc., a clinical-stage gene therapy company developing treatments for patients suffering from rare and life-threatening neurological genetic diseases, today reported topline results from the […]

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Know Your Resources: How Congressional Caseworkers Can Help You Obtain Insurance Coverage for New Therapies

March 15, 2017
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Your elected officials who represent you in Washington, D.C. have caseworkers in their regional and district offices in your communities. These caseworkers can help you […]

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