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Registration is Now Open for the 2017 SMA Researcher Meeting

November 18, 2016
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Registration is now open for industry and academic researchers to attend our 2017 SMA Researcher Meeting, which will be held June 29-July 1 at Disney […]

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Cure SMA Launches Insurance Coverage and Payment Policy Project

November 16, 2016
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Earlier this year, Cure SMA initiated an insurance coverage and payment policy project, in partnership with District Policy Group. The goal of this project is […]

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6th Annual South Florida Gala of Hope Inspires Familes and Supporters

November 11, 2016
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The 6th Annual South Florida Chapter Gala of Hope will be held on November 17, 2016, at Ferrari Maserati of Fort Lauderdale, Florida. The event […]

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Cure SMA Joins SMA Europe and TREAT-NMD for Meeting with EMA Regulators

November 10, 2016
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Cure SMA will be participating in a one-day workshop with The European Medicines Agency (EMA—the European equivalent of the FDA), SMA Europe and TREAT-NMD to […]

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Cure SMA to Host Webinar on the New Drug Application Process

November 9, 2016
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On Tuesday, December 6, Cure SMA will be hosting a one-hour webinar on the New Drug Application (NDA) process. The webinar will be held at […]

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Biogen and Ionis Community Statement on Interim Analysis of CHERISH (Type 2) Trial

November 7, 2016
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Biogen and Ionis Pharmaceuticals have provided the following community statement regarding the interim analysis of the CHERISH trial: Dear Members of the SMA Community, Today […]

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Biogen and Ionis Pharmaceuticals Announce SPINRAZA (nusinersen) Meets Primary Endpoint at Interim Analysis of Phase 3 CHERISH Study

November 7, 2016
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Biogen and Ionis Pharmaceuticals announced that SPINRAZA (nusinersen), an investigational treatment for spinal muscular atrophy (SMA), met the primary endpoint at the interim analysis of […]

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AveXis Announces Single-Arm Design for Pivotal Study of AVXS-101

November 1, 2016
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AveXis, Inc., a clinical-stage gene therapy company developing treatments for patients suffering from rare and life-threatening neurological genetic diseases, today announced that the planned pivotal […]

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Family Registration for the 2017 Annual SMA Conference is Now Open

November 1, 2016
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Registration is now open for the 2017 Annual SMA Conference! The conference will be held at Disney’s Contemporary Resort at Disney World in Orlando, FL, […]

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Spotlight Innovation Launches Development of STL-182 to Treat SMA

October 31, 2016
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Spotlight Innovation has obtained an exclusive, worldwide license to STL-182, a novel compound invented by Drs. Elliot Androphy at Indiana University and Kevin Hodgetts, director […]

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