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Sweet Success: Baking a Difference Returns for a Second Year

November 7, 2023
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Breaking and Baking News!   Get ready to dust off those aprons and preheat those ovens because Baking a Difference is back and better than […]

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Biogen Shares DEVOTE and RESPOND Study Updates

October 26, 2023
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Biogen recently shared that they have completed enrollment in the global DEVOTE and RESPOND clinical studies. Check out the full SMA Community Statement here.

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Genentech Shares 1-Year Primary Analysis from RAINBOWFISH

October 9, 2023
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Last week, Genentech, a member of the Roche Group,  presented positive results from the primary analysis of the ongoing RAINBOWFISH study assessing the efficacy and […]

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Novartis Gene Therapies SMA Community Update

October 5, 2023
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Dear SMA Community, It was a pleasure to be able to join so many of you at the Cure SMA Annual Conference in Orlando this […]

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Cure SMA on Capitol Hill – A Message from Allie Williams

October 4, 2023
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Hey, it’s Allie here from Oklahoma! I am privileged to serve on the Cure SMA Adult Advisory Council and am part of a group of […]

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SMA Highlights and Updates from Biogen

October 2, 2023
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Dear SMA Community, As we reflect on SMA Awareness Month, we take this opportunity to celebrate all those who are a part of the SMA […]

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Identifying Biomarkers of Spinal Muscular Atrophy for Further Development

September 28, 2023
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An important part of Cure SMA’s core mission is to carry out and support research that will improve the quality of life for all people […]

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NMD Pharma Initiates Phase II Trial for SMA

September 26, 2023
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NMD Pharma, a clinical-stage biotech company leading the development of novel first-in-class therapies for severe neuromuscular disorders, recently announced that the first SMA patient has […]

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Scholar Rock Announces Completion of Enrollment for the Phase 3 SAPPHIRE Trial

September 19, 2023
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Today, Scholar Rock announced that enrollment in their Phase 3 SAPPHIRE trial is now complete. The Phase 3 trial will evaluate the safety and efficacy of […]

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Biohaven Completes Enrollment in Pivotal Phase 3 Study

September 19, 2023
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Recently, Biohaven released a statement on the completed enrollment of their pivotal Phase 3 Study of Taldefgrobep Alfa in people with SMA. Check out Biohaven’s […]

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