Front Page News
AveXis Releases New Data on Phase 1 Clinical Trial
AveXis has released new data from their current Phase 1 clinical trial testing AVXS-101, a systemic delivery of gene therapy for SMA. The data from […]
Read More ›Record Number of Abstracts Submitted for the 2016 SMA Researcher Meeting
Abstract submission is now closed for the 2016 SMA Researcher Meeting. We are excited to announce that we received 118 submissions, a record number. Our […]
Read More ›Senate HELP Committee Passes Another 7 Innovation Bills
The Senate Health, Education, Labor and Pensions (HELP) Committee yesterday passed an additional 7 bills out of committee. Along with the 7 bills previously passed […]
Read More ›Winter 2015 Issue of Directions Now Online
The Winter 2015 issue of Directions is now available! Please visit our Support & Care Publications page to download this issue or past issues of […]
Read More ›Cure SMA-Funded Researchers Publish Paper on Motor Neuron and Astrocyte Defects
Cure SMA-funded researcher Chien-Ping Ko has published a paper in the Journal of Neuroscience, called “Defects in Motoneuron–Astrocyte Interactions in Spinal Muscular Atrophy.” The research […]
Read More ›2016 Annual SMA Conference on Track to Break Attendance Records
Registration for the Annual SMA Conference is well on its way to a record-setting number. Over 700 families and researchers have registered for the conference […]
Read More ›Cure SMA Awards $140,000 Grant to Rashmi Kothary, MD, Ottawa Hospital Research Institute
Cure SMA has awarded a $140,000 research grant to Rashmi Kothary, MD, at the Ottawa Hospital Research Institute for his project, ” Muscle satellite cell […]
Read More ›Cure SMA Awards $140,000 Grant to Megerditch Kiledjian, PhD, of Rutgers
Cure SMA has awarded a $140,000 research grant to Megerditch Kiledjian, PhD, at Rutgers, The State University of New Jersey, for his project, “Novel Strategies […]
Read More ›Senate HELP Committee Passes Innovation Bills
The Senate Health, Education, Labor and Pensions (HELP) Committee has passed 7 bills out of committee as part of its “step-by-step” approach to Innovation and […]
Read More ›Update on 21st Century Cures/Innovation: the Senate’s “Step-by-Step” Approach
Cure SMA has been carefully monitoring the consideration of 21st Century Cures on Capitol Hill. As you know, the House passed legislation in July last […]
Read More ›