Front Page News

Cure SMA Awards $140,000 Grant to Megerditch Kiledjian, PhD, of Rutgers

February 11, 2016
Posted in , ,

Cure SMA has awarded a $140,000 research grant to Megerditch Kiledjian, PhD, at Rutgers, The State University of New Jersey, for his project, “Novel Strategies […]

Read More ›

Senate HELP Committee Passes Innovation Bills

February 9, 2016
Posted in ,

The Senate Health, Education, Labor and Pensions (HELP) Committee has passed 7 bills out of committee as part of its “step-by-step” approach to Innovation and […]

Read More ›

Update on 21st Century Cures/Innovation: the Senate’s “Step-by-Step” Approach

February 2, 2016
Posted in ,

Cure SMA has been carefully monitoring the consideration of 21st Century Cures on Capitol Hill. As you know, the House passed legislation in July last […]

Read More ›

Cure SMA-Funded Researcher Publishes Paper on Biomarker Study

January 21, 2016
Posted in , ,

Cure SMA-funded researcher Stephen Kolb has published a paper in the journal Annals of Clinical and Translational Neurology. This paper reported on the baseline results […]

Read More ›

Cure SMA Testifies Before FDA at PDUFA Meeting

January 19, 2016
Posted in , ,

The Prescription Drug User Fee Act (PDUFA), the law that allows the FDA to collect fees from drug manufacturers to fund the new drug approval […]

Read More ›

Cure SMA Receives Generous Donation from Fighting for Kaiden Foundation

January 13, 2016
Posted in , ,

Cure SMA would like to thank the Fighting for Kaiden Foundation for their generous donations to Cure SMA programs. That generosity is providing both support […]

Read More ›

Biogen and Ionis Provide Update on Nusinersen (IONIS-SMNRx)

January 11, 2016
Posted in ,

Biogen and Ionis Pharmaceuticals recently provided an update on the clinical development of nusinersen (IONIS-SMNRx), which is currently being tested in Phase 3 clinical trials: […]

Read More ›

Abstract Submission Opens for 2016 SMA Researcher Meeting

January 8, 2016
Posted in , ,

Abstract submission is now open for the 2016 SMA Researcher Meeting, which will be held June 16-18 as part of the Annual SMA Conference in […]

Read More ›

Roche Announces New Clinical Trial of RG7916

January 5, 2016
Posted in ,

Roche, along with partners PTC Therapeutics and the SMA Foundation, recently provided the following update on the development of RG7800 and on a new clinical […]

Read More ›

AveXis Announces the Completion of Enrollment for Phase 1 Gene Therapy Trial

January 4, 2016
Posted in ,

AveXis has announced that they have completed enrollment in a Phase 1 study testing systemic delivery of gene therapy for SMA. The trial has enrolled […]

Read More ›
Scroll to Top