Front Page News
Cure SMA Awards $140,000 Grant to Megerditch Kiledjian, PhD, of Rutgers
Cure SMA has awarded a $140,000 research grant to Megerditch Kiledjian, PhD, at Rutgers, The State University of New Jersey, for his project, “Novel Strategies […]
Read More ›Senate HELP Committee Passes Innovation Bills
The Senate Health, Education, Labor and Pensions (HELP) Committee has passed 7 bills out of committee as part of its “step-by-step” approach to Innovation and […]
Read More ›Update on 21st Century Cures/Innovation: the Senate’s “Step-by-Step” Approach
Cure SMA has been carefully monitoring the consideration of 21st Century Cures on Capitol Hill. As you know, the House passed legislation in July last […]
Read More ›Cure SMA-Funded Researcher Publishes Paper on Biomarker Study
Cure SMA-funded researcher Stephen Kolb has published a paper in the journal Annals of Clinical and Translational Neurology. This paper reported on the baseline results […]
Read More ›Cure SMA Testifies Before FDA at PDUFA Meeting
The Prescription Drug User Fee Act (PDUFA), the law that allows the FDA to collect fees from drug manufacturers to fund the new drug approval […]
Read More ›Cure SMA Receives Generous Donation from Fighting for Kaiden Foundation
Cure SMA would like to thank the Fighting for Kaiden Foundation for their generous donations to Cure SMA programs. That generosity is providing both support […]
Read More ›Biogen and Ionis Provide Update on Nusinersen (IONIS-SMNRx)
Biogen and Ionis Pharmaceuticals recently provided an update on the clinical development of nusinersen (IONIS-SMNRx), which is currently being tested in Phase 3 clinical trials: […]
Read More ›Abstract Submission Opens for 2016 SMA Researcher Meeting
Abstract submission is now open for the 2016 SMA Researcher Meeting, which will be held June 16-18 as part of the Annual SMA Conference in […]
Read More ›Roche Announces New Clinical Trial of RG7916
Roche, along with partners PTC Therapeutics and the SMA Foundation, recently provided the following update on the development of RG7800 and on a new clinical […]
Read More ›AveXis Announces the Completion of Enrollment for Phase 1 Gene Therapy Trial
AveXis has announced that they have completed enrollment in a Phase 1 study testing systemic delivery of gene therapy for SMA. The trial has enrolled […]
Read More ›