Front Page News
Cure SMA to Host Clinical and Regulatory Webinar
On Monday, November 9, Cure SMA will be hosting a one-hour webinar on clinical trials and regulatory topics. The webinar will be held at 11:00am […]
Read More ›PTC Announces New Clinical Trial Results at World Muscle Congress
PTC Therapeutics, in partnership with Roche and the SMA Foundation, recently announced new results from their ongoing Phase 2 trial of RG7800, a small molecule […]
Read More ›Community Update on ISIS-SMNRx from Biogen and Isis
Biogen and Isis Pharmaceuticals recently provided an update on the clinical development of ISIS-SMNRx, which is currently being tested in Phase 3 clinical trials: Dear […]
Read More ›New Gene Therapy Results Announced at World Muscle Congress
Nationwide Children’s Hospital/AveXis recently announced new results from their ongoing Phase 1 trial of systemic gene therapy for SMA. Dr. Jerry R. Mendell, Director of […]
Read More ›Registration Open for the 2016 SMA Researcher Meeting
Registration is now open for industry and academic researchers to attend our 2016 SMA Researcher Meeting, which will be held June 16-18 in Anaheim, CA, […]
Read More ›House of Representatives Passes Ensuring Access to Clinical Trials Act
The House of Representatives has passed the Ensuring Access to Clinical Trials Act of 2015 (EACT). This bill already passed the Senate in July, and […]
Read More ›Thank You to Jessica Moyer and Family
A note from Rich Rubenstein, Kenneth Hobby, and the entire Cure SMA team: Cure SMA has had the honor to have Jessica Moyer and her […]
Read More ›FDA Engagement Update: The Voices of SMA
Thanks to our vibrant community, August was one of our largest and best awareness months ever, with unprecedented levels of public awareness and outreach for […]
Read More ›2015 SMA Researcher Meeting Summary: SMN Partners and Targets, Part 2
We will be posting a series of summaries from our 2015 researcher meeting, highlighting some of the most interesting new developments and discoveries presented there. […]
Read More ›2015 SMA Researcher Meeting Summary: SMN Partners and Targets, Part 1
We will be posting a series of summaries from our 2015 researcher meeting, highlighting some of the most interesting new developments and discoveries presented there. […]
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