Front Page News
2015 Annual SMA Conference Exhibitors
Thank you to the following exhibitors who have generously supported our 2015 Annual SMA Conference. This one-of-a-kind event would not be possible without your support! […]
Read More ›Cure SMA Releases New Clinical Trial Care Series Booklet
As more and more SMA drug programs progress through clinical trials, there is an increasing need for accurate and unbiased information on clinical trials from […]
Read More ›Isis Releases Encouraging Results from Phase 2 Study
Isis Pharmaceuticals provided an update on its ongoing open-label Phase 2 clinical study of ISIS-SMNRx in infants with Type I spinal muscular atrophy (SMA). Previously […]
Read More ›SMA Drug Pipeline Grows to 18 Programs
We’ve recently released an update to our SMA drug pipeline. This latest version shows the continued growth of the pipeline, setting several new marks for […]
Read More ›Spring 2015 Directions Posted Online
The Spring 2015 issue of Directions, our biannual family support newsletter, builds our community by sharing stories and experiences. Families from all over the world […]
Read More ›Biogen Announces EMBRACE, a New Phase 2 Clinical Trial
Biogen, in partnership with Isis Pharmaceuticals, has announced a new Phase 2 clinical trial, called EMBRACE. EMBRACE is a multi-center, Phase 2 clinical study evaluating […]
Read More ›2015 Annual SMA Conference Booklet Now Posted
The 2015 Annual SMA Conference Booklet has been posted. The booklet includes: A complete schedule, including information about the special events we’ve got planned for […]
Read More ›High School Students Lead the Way at Concert for a Cure
The 15th Annual Concert for a Cure was held on Saturday, May 9, 2015, a the Diablo Country Club in Danville, CA and was a […]
Read More ›Novartis Launches Phase 2 Clinical Trial
Novartis has published a paper in the journal Nature Chemical Biology, detailing promising results in their program to develop an orally available SMA drug that […]
Read More ›Cure SMA Announces Partnership with The District Policy Group
Cure SMA has announced a new partnership with the District Policy Group, a boutique lobbying, public policy, and advocacy practice, to advocate for several key […]
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