Front Page News
Isis Releases Encouraging Results from Phase 2 Study
Isis Pharmaceuticals provided an update on its ongoing open-label Phase 2 clinical study of ISIS-SMNRx in infants with Type I spinal muscular atrophy (SMA). Previously […]
Read More ›SMA Drug Pipeline Grows to 18 Programs
We’ve recently released an update to our SMA drug pipeline. This latest version shows the continued growth of the pipeline, setting several new marks for […]
Read More ›Spring 2015 Directions Posted Online
The Spring 2015 issue of Directions, our biannual family support newsletter, builds our community by sharing stories and experiences. Families from all over the world […]
Read More ›Biogen Announces EMBRACE, a New Phase 2 Clinical Trial
Biogen, in partnership with Isis Pharmaceuticals, has announced a new Phase 2 clinical trial, called EMBRACE. EMBRACE is a multi-center, Phase 2 clinical study evaluating […]
Read More ›2015 Annual SMA Conference Booklet Now Posted
The 2015 Annual SMA Conference Booklet has been posted. The booklet includes: A complete schedule, including information about the special events we’ve got planned for […]
Read More ›High School Students Lead the Way at Concert for a Cure
The 15th Annual Concert for a Cure was held on Saturday, May 9, 2015, a the Diablo Country Club in Danville, CA and was a […]
Read More ›Novartis Launches Phase 2 Clinical Trial
Novartis has published a paper in the journal Nature Chemical Biology, detailing promising results in their program to develop an orally available SMA drug that […]
Read More ›Cure SMA Announces Partnership with The District Policy Group
Cure SMA has announced a new partnership with the District Policy Group, a boutique lobbying, public policy, and advocacy practice, to advocate for several key […]
Read More ›15th Annual New England Walk-n-Roll Raises Over $100,000
The 15th Annual New England Chapter Walk-n-Roll was held on Saturday, May 16, at beautiful DCR Wompatuck Park in Hingham, MA. The sun was shining […]
Read More ›Cure SMA Receives NIH Grant
For the seventh consecutive year, Cure SMA has received a grant from the National Institutes of Health (NIH) for the SMA Researcher Meeting. This year’s […]
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