Front Page News
Update on Clinical Development of RG7800
F. Hoffman-La Roche, PTC and the SMA Foundation recently provided an update on the clinical development of RG7800, an investigational SMN2 splicing modifier that is […]
Read More ›Cure SMA Funds $1.85 Million in New Research Grants in 2014-2015
Over the past few months, Cure SMA has announced a total of $1.85 million in new research funding. Our model is designed to fund both […]
Read More ›Cure SMA Announces Additional $445,000 for Nationwide Children’s Hospital Gene Therapy Program led by Brian Kaspar, PhD
Cure SMA, the leading organization dedicated to the treatment and cure of spinal muscular atrophy (SMA), recently provided an additional $445,000 grant toward a gene […]
Read More ›New 21st Century Cures Discussion Draft Released
The US House of Representatives Energy and Commerce Committee has released a new 21st Century Cures discussion draft. This is a revised and expanded version […]
Read More ›Registration for the 2015 Annual SMA Conference Closes in Two Weeks
The deadline to register for our Annual SMA Conference is just two weeks away. Registration will close on Friday, May 9. Over 1,000 people have […]
Read More ›Cure SMA Publishes New Care Series Booklet on Musculoskeletal System
Cure SMA has recently released an updated version of our latest care series booklet, The Musculoskeletal System. As with all our care series booklets, The […]
Read More ›Spring 2015 Issue of Compass Now Available
The Spring 2015 issue of Compass is now available online. As part of our most recent round of funding, we made five grants totaling $640,000 […]
Read More ›Annual SMA Conference to Feature Panel of Leading SMA Drug Experts
The Annual SMA Conference will bring together well over a thousand families and researchers from around the world. During the conference, several sessions are set […]
Read More ›Muscles for Mckenna Gala Raises Over $100,000
Held Friday, March 13, in Philadelphia, the 3rd Annual Muscles for Mckenna Gala has raised an incredible $107,000, and organizers are continuing to take donations […]
Read More ›Cure SMA Welcomes the Virginia Chapter
Cure SMA is pleased to announce the creation of a new chapter in Virginia. This chapter will also serve residents of Washington DC. Led by […]
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