Front Page News
Cure SMA Provides Record Number of Resources to Families Worldwide
Along with funding spinal muscular atrophy research, Cure SMA provides thousands of families with vital family support and resources to help them live active, engaged […]
Read More ›Cure SMA Funding Leads to 16 New Research Publications in 2014
An important goal of our research funding strategy is to share scientific findings with the broader scientific community. Scientists who receive Cure SMA funding often […]
Read More ›Hope on the Hill Advances Key SMA Legislative Priorities
This year’s 4th Annual Hope on the Hill Congressional Dinner in Washington D.C. was a great success. Building on of this year’s Annual SMA Conference—also […]
Read More ›Cure SMA Funds 26 Research Projects in 2014
Our strategic research approach includes four areas—basic research, drug discovery, clinical trials, and clinical care—working together toward our vision of a world without SMA. Cure […]
Read More ›Isis Expands Phase 3 Clinical Trials
Isis recently announced that they have tested the first patient in CHERISH, a multi-center Phase 3 clinical study evaluating the efficacy and safety of the […]
Read More ›Cure SMA Researchers Present at Society for Neuroscience Meeting
The Society for Neuroscience (SfN) Meeting is the premiere neurobiology meeting, with over 30,000 scientists in attendance each year. This year’s meeting was held November […]
Read More ›PTC Therapeutics Announces New Phase 1a/2b Clinical Trial
PTC Therapeutics, Inc. announced today that its joint development program in Spinal Muscular Atrophy (SMA) with Roche and the SMA Foundation (SMAF) has started a […]
Read More ›Isis Announces Second Phase III Clinical Trial
Isis recently announced the start of CHERISH, a multi-center Phase III clinical study evaluating the efficacy and safety of the investigational compound, ISIS-SMNRx, in non-ambulatory […]
Read More ›Southern California Gala of Hope Brings Community and Industry Partners Together to Raise $80,000
On November 15, 140 guests gathered for the Inaugural Southern California Cure SMA Gala of Hope. This fantastic evening raised over $80,000 in support of […]
Read More ›Cure SMA Scientific Advisory Board Meets in Washington D.C.
Today and tomorrow, Cure SMA’s Scientific Advisory Board (SAB) will be meeting in Washington D.C. Our Scientific Advisory Board is a recognized group of experts […]
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