Industry Updates

Genentech Shares New Evrysdi Data on Improved Motor Function and Survival in Babies with SMA Type 1

April 21, 2021
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Genentech, a member of the Roche Group, has shared new 2-year data from Part 2 of FIREFISH, a Phase 2/3 global study evaluating Evrysdi (risdiplam) […]

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Biogen Shares New Spinraza Data Exploring Opportunities to Improve Outcomes for SMA Patients

April 21, 2021
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Biogen has shared new data from the Spinraza (nusinersen) clinical development program aimed at optimizing outcomes for people with SMA and advancing understanding of the […]

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Scholar Rock Community Statement on TOPAZ 12-Month Topline Data

April 6, 2021
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Scholar Rock provided the below community statement on data for apitegromab (SRK-015) following the distribution of this company press release.  Dear Members of the SMA […]

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Community Statement from Genentech

March 18, 2021
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Dear SMA Community, Based on our commitment to the SMA community to provide transparent, timely updates related to our medicines, we are writing to share […]

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Community Statement from Novartis Gene Therapies

March 18, 2021
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Dear Cure SMA Community, Novartis Gene Therapies is committed to patient safety and the ongoing monitoring of adverse events as it relates to the use […]

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