Latest News
Cure SMA Awards $140,000 Grant to Christine DiDonato, PhD, Ann & Robert H. Lurie Children’s Hospital of Chicago
Cure SMA has awarded a $140,000 research grant to Christine DiDonato, PhD, Ann & Robert H. Lurie Children’s Hospital of Chicago, for her project, “Skeletal muscle activators as potential modulators […]
Read More ›Biogen Releases New Data from Cherish and Nurture Trials
Biogen will present Phase 3 end of study SPINRAZA® (nusinersen) data from CHERISH, which demonstrated a highly statistically significant and clinically meaningful improvement in motor function in children with later-onset […]
Read More ›SMA Community’s Voice Heard “Loud and Clear” at Last Week’s Patient Focused Drug Development Meeting with the FDA
On April 18, 2017, the SMA community—families, clinicians, researchers, industry and regulators—gathered for a Patient-Focused Drug Development (PFDD) Meeting with the FDA. As part of the reauthorization of the Prescription […]
Read More ›Cure SMA to Host Webinar on Spinraza Access, as List of Administration Sites is Released
On Thursday, May 4, at 1:00pm EST (10:00am PST/11:00am MST/12:00pm CST), Cure SMA will hold a webinar updating the community on the status of Spinraza access. Among the topics covered […]
Read More ›The European Medicines Agency (EMA) Recommends Granting Marketing Authorization in the European Union for Spinraza
The European Medicines Agency (EMA) has recommended granting a marketing authorization in the European Union (EU) for Spinraza. The recommendation indicates that Spinraza should be covered for all types of […]
Read More ›Cure SMA Awards $75,000 Grant to Jean Giacomotto, PhD, University of Queensland, Australia
Cure SMA has awarded a $75,000 research grant to Jean Giacomotto, PhD, at the University of Queensland, for his project, “Zebrafish models of Spinal Muscular Atrophy optimized for chemical genetics […]
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