Latest News
Cure SMA Releases June 2016 Update to the SMA Drug Pipeline
We’ve recently released an update to the SMA drug pipeline. This latest version includes: 18 active programs. 14 pharmaceutical partners. 6 programs in clinical trials. 28 programs in the cumulative […]
Read More ›Thank you to Our 2016 Annual SMA Conference Exhibitors!
Thank you to the following exhibitors who have generously supported our 2016 Annual SMA Conference. This one-of-a-kind event would not be possible without your support! For more information on any […]
Read More ›Biogen and Ionis Release Spring 2016 Community Update
Biogen and Ionis Pharmaceuticals recently provided an update on the clinical development of nusinersen (IONIS-SMNRx), which is currently being tested in Phase 3 clinical trials: Dear members of the SMA […]
Read More ›2016 Update on SMA-FDA Interactions
The SMA drug pipeline has grown dramatically in just over a decade. Of the 18 programs in the pipeline, six of these are in clinical trials, and several of those […]
Read More ›2016 Annual SMA Conference Booklet Now Posted
The 2016 Annual SMA Conference Booklet has been posted. The booklet includes: A complete schedule with information about the special events we’ve got planned for each evening including: the Meet […]
Read More ›Update on the Clinical Development of LMI070
Novartis recently provided the following update on clinical trials for LMI070, an orally available SMA drug that corrects SMN2 splicing: “We have made the difficult decision to pause enrollment for […]
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