Latest News
Isis Releases Encouraging Results from Phase 2 Study
Isis Pharmaceuticals provided an update on its ongoing open-label Phase 2 clinical study of ISIS-SMNRx in infants with Type I spinal muscular atrophy (SMA). Previously the company reported data from […]
Read More ›SMA Drug Pipeline Grows to 18 Programs
We’ve recently released an update to our SMA drug pipeline. This latest version shows the continued growth of the pipeline, setting several new marks for both breadth and depth: We […]
Read More ›Spring 2015 Directions Posted Online
The Spring 2015 issue of Directions, our biannual family support newsletter, builds our community by sharing stories and experiences. Families from all over the world connect with each other through […]
Read More ›Biogen Announces EMBRACE, a New Phase 2 Clinical Trial
Biogen, in partnership with Isis Pharmaceuticals, has announced a new Phase 2 clinical trial, called EMBRACE. EMBRACE is a multi-center, Phase 2 clinical study evaluating the safety and exploratory efficacy […]
Read More ›2015 Annual SMA Conference Booklet Now Posted
The 2015 Annual SMA Conference Booklet has been posted. The booklet includes: A complete schedule, including information about the special events we’ve got planned for each evening. Times, locations, details, […]
Read More ›High School Students Lead the Way at Concert for a Cure
The 15th Annual Concert for a Cure was held on Saturday, May 9, 2015, a the Diablo Country Club in Danville, CA and was a tremendous success raising over $150,000 […]
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