Latest News
2015 Annual SMA Conference Exhibitors
Thank you to the following exhibitors who have generously supported our 2015 Annual SMA Conference. This one-of-a-kind event would not be possible without your support! For more information on any […]
Read More ›Cure SMA Releases New Clinical Trial Care Series Booklet
As more and more SMA drug programs progress through clinical trials, there is an increasing need for accurate and unbiased information on clinical trials from our community. Cure SMA has […]
Read More ›Isis Releases Encouraging Results from Phase 2 Study
Isis Pharmaceuticals provided an update on its ongoing open-label Phase 2 clinical study of ISIS-SMNRx in infants with Type I spinal muscular atrophy (SMA). Previously the company reported data from […]
Read More ›SMA Drug Pipeline Grows to 18 Programs
We’ve recently released an update to our SMA drug pipeline. This latest version shows the continued growth of the pipeline, setting several new marks for both breadth and depth: We […]
Read More ›Spring 2015 Directions Posted Online
The Spring 2015 issue of Directions, our biannual family support newsletter, builds our community by sharing stories and experiences. Families from all over the world connect with each other through […]
Read More ›Biogen Announces EMBRACE, a New Phase 2 Clinical Trial
Biogen, in partnership with Isis Pharmaceuticals, has announced a new Phase 2 clinical trial, called EMBRACE. EMBRACE is a multi-center, Phase 2 clinical study evaluating the safety and exploratory efficacy […]
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