Latest News
PTC Therapeutics Announces New Phase 1a/2b Clinical Trial
PTC Therapeutics, Inc. announced today that its joint development program in Spinal Muscular Atrophy (SMA) with Roche and the SMA Foundation (SMAF) has started a Phase 1b/2a study in adult […]
Read More ›Isis Announces Second Phase III Clinical Trial
Isis recently announced the start of CHERISH, a multi-center Phase III clinical study evaluating the efficacy and safety of the investigational compound, ISIS-SMNRx, in non-ambulatory children with Spinal Muscular Atrophy […]
Read More ›Southern California Gala of Hope Brings Community and Industry Partners Together to Raise $80,000
On November 15, 140 guests gathered for the Inaugural Southern California Cure SMA Gala of Hope. This fantastic evening raised over $80,000 in support of Cure SMA. Our thanks to […]
Read More ›Cure SMA Scientific Advisory Board Meets in Washington D.C.
Today and tomorrow, Cure SMA’s Scientific Advisory Board (SAB) will be meeting in Washington D.C. Our Scientific Advisory Board is a recognized group of experts in SMA and motor neuron […]
Read More ›Families, Government, and Industry Leaders Unite to Help Cure SMA
This year’s 4th Annual Hope on the Hill Congressional Dinner in Washington D.C. is less than three weeks away. At Cure SMA, we know that no single group can develop […]
Read More ›Together, We Can Cure SMA
Cure SMA is our name, and it’s also our rallying cry. It’s why we keep funding research and family support. And we know it’s why our community gives so much […]
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