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Funding Process Reaches Next Steps for Spinal Muscular Atrophy Clinical Care Research
At the end of last week, we announced the close of our for request for proposals (RFP) for clinical care research. A clinical care RFP is an invitation for scientists […]
Read More ›Chef Takashi Competes for Cure SMA
Did you catch Cure SMA on Top Chef last week? Chef Takashi Yagihashi competed on behalf of Cure SMA for Bravo’s Top Chef Duels series. What a great opportunity to […]
Read More ›Cure SMA Featured in Assay and Drug Development Technologies
Cure SMA was featured in the July/August issue of Assay and Drug Development Technologies, a scientific journal that focuses on the development of new drugs. In honor of SMA Awareness […]
Read More ›Spinal Muscular Atrophy Mice Model Results Published in the Journal Science
On August 7, the journal Science published results of a preclinical study demonstrating that treatment with orally available RNA splicing modifiers of the SMN2 gene starting early after birth prevents […]
Read More ›Trophos Presents Pivotal Phase II/III Study Results on Olesoxime in Spinal Muscular Atrophy at The American Academy of Neurology Meeting
Originally published on April 29, 2014 The 66th American Academy of Neurology (AAN) Meeting is being held this week in Philadelphia. Over 10,000 neurologists are in attendance. Trophos presented late […]
Read More ›Isis Presents Update on Spinal Muscular Atrophy Drug Trials at the American Academy of Neurology Meeting
Originally published on April 29, 2014 Isis Pharmaceuticals, Inc. today provided an update on both of its ongoing open-label Phase 2 clinical studies of ISIS-SMNRx in infants and children with spinal […]
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