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District of Columbia Starts Screening for SMA During Rare Disease Month

February 22, 2023
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Cure SMA is pleased to announce that the District of Columbia (DC) is now screening babies born in DC for spinal muscular atrophy (SMA). The DC Department of Health (DC […]

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NEW REPORT: SMA Community Describes Air Travel Experiences as “Good, but mostly Bad, and Ugly”

February 16, 2023
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Despite federal laws and protections aimed at improving air travel for people with disabilities, a new report from Cure SMA highlights that the air travel experience for most individuals and […]

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Cure SMA Awards $150,000 Grant to Florence Rage, PhD, at the Institute of Molecular Genetics of Montpellier

February 15, 2023
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Florence Rage, PhD, was awarded $150,000 for her research project, “Deciphering the Mechanisms of RNA Transport along Axons to Understand the Progression of Spinal Muscular Atrophy (SMA).” Dr. Rage’s basic […]

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Cure SMA Awards $150,000 Grant to Anton Blatnik, PhD, at The Ohio State University

February 8, 2023
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Anton Blatnik, PhD, at The Ohio State University has been awarded $150,000 for his research project, “Determining Primary Splicing Changes in Spinal Muscular Atrophy.” Dr. Blatnik’s basic research grant is […]

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Cure SMA Supports Clinical Trial Readiness

January 26, 2023
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In recent years, the FDA-approval of three new SMA treatments has made it possible for a growing number of affected individuals to receive disease-modifying drugs. In addition, many more potential […]

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Cure SMA Awards $150,000 Grant to Alberto Kornblihtt, PhD, Universidad de Buenos Aires

January 26, 2023
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Each year, Cure SMA invites scientists from around the world to submit funding proposals for basic research projects that address specific unanswered questions in SMA biology. Our Scientific Advisory Board […]

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