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SMA Community Seeks SSI Improvements on Program’s 50th Anniversary

October 30, 2022
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Fifty years ago today, the Supplemental Security Income (SSI) program was created to “provide supplemental security income to individuals who have attained age 65 or are blind or disabled” for […]

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New Phase 2 TOPAZ Trial Data Indicate Positive Trends in Quality-of-Life Measures Over 24 Months with Apitegromab for Nonambulatory Patients with Types 2 and 3 SMA

October 25, 2022
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Scholar Rock yesterday announced new quality-of-life (QoL) data from its Phase 2 TOPAZ trial extension period evaluating patient outcomes after 24 months of treatment which indicate stabilization or continued improvement […]

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Community Spotlight: Amber-Joi Watkins and Family

October 5, 2022
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The Igbo and Yoruba proverb, “It takes a village to raise a child” has been in use for centuries and remains in use across languages and cultures due to its […]

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Cure SMA Holds Patient-Led Listening Session with FDA

October 4, 2022
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On Thursday, August 4, 2022, six members of the SMA community had the opportunity to talk directly with the U.S. Food and Drug Administration (FDA) about their lived experiences with […]

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A Deliciously Easy Way to Fundraise for Cure SMA

October 4, 2022
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Nothing brings people together more than sharing a meal, but what if you could make that meal even more meaningful? We’re encouraging all members of our SMA community to consider […]

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Cure SMA Holds Patient-Led Listening Session with FDA

October 4, 2022
Posted in , ,

On Thursday, August 4, 2022, six members of the SMA community had the opportunity to talk directly with the U.S. Food and Drug Administration (FDA) about their lived experiences with […]

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