Latest News
Genentech, Roche and PTC Therapeutics Provide Update on Regulatory Filing for Risdiplam
On January 7th, PTC Therapeutics, Inc. provided a corporate update, which will be detailed as part of the company’s presentation at the 37th Annual J.P. Morgan Healthcare Conference. As part […]
Read More ›Teen and Young Adult Survey Extended Through January 21st
Are you or a family member between the ages of 12 and 25? Do you want to share your opinion on living with SMA and what is important to you […]
Read More ›Community Spotlight: The Jankowski Family
It has been a little over two years since doctors told Chris and Kelly Jankowski that their first-born son, William, had spinal muscular atrophy (SMA) type I. In the immediate […]
Read More ›Cure SMA Announces Expanded Phase 3 of SMA Industry Collaboration
Cure SMA is pleased to announce the launch of an expanded Phase 3 of our SMA Industry Collaboration. The SMA Industry Collaboration is a multi-faceted partnership that brings together pharmaceutical […]
Read More ›Hope on the Hill Congressional Dinner Raises $200,000
The 8th Annual “Hope on the Hill” Congressional Dinner was held on Tuesday, November 27, 2018 at The Willard Hotel in Washington, DC. More than 170 people from the SMA […]
Read More ›December Webinar on SMA Treatments and Clinical Trials Now Available Online
A recording of the December 13th webinar updating the community on SMA treatments and clinical trials is now available online. A PDF of the webinar presentation is also available for […]
Read More ›