Latest News
Fall 2017 Directions Now Available for Download
The Fall 2017 issue of Directions is now available. Please visit our Support & Care Publications page to download this issue or past issues of Directions. Our biannual newsletter builds […]
Read More ›2017 Research Year-in-Review
Over our past fiscal year—from July 1, 2016, to June 30, 2017—Cure SMA has funded 28 projects with over $2.5 million in new research funding. This funding will be used […]
Read More ›Cure SMA Advocates Continue to Advance Newborn Screening Efforts
SMA advocates across the country are working tirelessly with Cure SMA to educate state decision makers on newborn screening. In Maryland and Minnesota, the states’ Newborn Screening Advisory Committees voted […]
Read More ›AveXis Announces Plan to Initiate Phase 1 Trial in SMA Type 2 Utilizing Intrathecal Delivery of AVXS-101
AveXis, Inc., a clinical-stage gene therapy company developing treatments for patients suffering from rare and life-threatening neurological genetic diseases, today announced the U.S. Food and Drug Administration (FDA) has notified […]
Read More ›Adult Scholarships Offered for the 2018 Annual SMA Conference
Cure SMA is pleased to offer scholarships to the 2018 Annual SMA Conference for all adults with SMA, thanks to a generous grant from The Dhont Family Foundation. The scholarship […]
Read More ›Cure SMA-Funded Research Results in 21 Published Journal Articles
An important goal of our research funding strategy is to share scientific findings with the broader scientific community. To help accomplish this goal, scientists who receive Cure SMA funding often […]
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