Our Impact
NIH Releases Summary of the SO-SMART Workshop
During the Annual SMA Conference in Washington DC this past June, the National Institutes of Health (NIH) hosted a workshop on clinical trial design in […]
Read More ›Help Us Make History with $750,000 for SMA Research
Just over a month ago, we announced a year-end goal of $540,000 to help fund SMA research and family support. Thanks to the generosity of […]
Read More ›Cure SMA Provides Record Number of Resources to Families Worldwide
Along with funding spinal muscular atrophy research, Cure SMA provides thousands of families with vital family support and resources to help them live active, engaged […]
Read More ›Cure SMA Funding Leads to 16 New Research Publications in 2014
An important goal of our research funding strategy is to share scientific findings with the broader scientific community. Scientists who receive Cure SMA funding often […]
Read More ›Cure SMA Funds 26 Research Projects in 2014
Our strategic research approach includes four areas—basic research, drug discovery, clinical trials, and clinical care—working together toward our vision of a world without SMA. Cure […]
Read More ›SMA Drug Pipeline Continues to Grow
This is an exciting time for the entire SMA community, as we celebrate another year of increasing momentum toward our goal of a treatment and […]
Read More ›Cure SMA Scientific Advisory Board Meets in Washington D.C.
Today and tomorrow, Cure SMA’s Scientific Advisory Board (SAB) will be meeting in Washington D.C. Our Scientific Advisory Board is a recognized group of experts […]
Read More ›Families, Government, and Industry Leaders Unite to Help Cure SMA
This year’s 4th Annual Hope on the Hill Congressional Dinner in Washington D.C. is less than three weeks away. At Cure SMA, we know that […]
Read More ›Medical Advisory Council Gathers for Fall 2014 Meetings
Members of the Cure SMA Medical Advisory Council (MAC) are holding two days of meetings, November 7-8, at the Cure SMA national offices. The MAC […]
Read More ›Promising Results Published on Cure SMA-Funded Gene Therapy Project
A manuscript from the laboratory of Dr. Brian Kaspar of Nationwide Children’s Hospital was recently published in the journal Molecular Therapy. The paper, “Improving single […]
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