Our Impact
The Discovery of Spinraza
SMA is caused by a mutation in the survival motor neuron gene 1 (SMN1). In a healthy person, this gene produces a protein—called survival motor […]
Read More ›There is Still Time to Complete Cure SMA’s 2018 Community Survey
Dear Members of the SMA Community, For the past several years, we’ve been working to collect data and information on our community’s experiences, goals, hopes, […]
Read More ›Cure SMA Awards $150,000 Grant to Bakri Elsheikh, MD, Ohio State University Wexner Medical Center
Cure SMA has awarded a $150,000 research grant to Bakri Elsheikh, MD, at the Ohio State University Wexner Medical Center, for his project, “Determine the […]
Read More ›Cure SMA Database Findings Published in the Journal of Neuromuscular Diseases
An important goal at Cure SMA is to collect data to better understand the SMA patient population, and then to report this data back to […]
Read More ›SMA Newborn Screening Guidelines Published in Journal of Neuromuscular Diseases
The recent decision of the federal Advisory Committee on Heritable Disorders in Newborns and Children (ACHDNC) to recommend SMA for addition to the RUSP, as […]
Read More ›Cure SMA Welcomes Back AveXis as a 2018 National Premier Partner
Cure SMA is excited to announce that AveXis is returning as a National Premier Partner for 2018. As part of their partnership, AveXis is generously […]
Read More ›Cure SMA Awards $150,000 Grant to Brunhilde Wirth, PhD, Institute of Cologne, Germany
Cure SMA has awarded a $150,000 research grant to Brunhilde Wirth, PhD, at Institute of Cologne, Germany, for her project, “Study of combinatorial therapy based […]
Read More ›Cure SMA Awards $50,000 Grant to Rashmi Kothary, PhD, University of Ottawa
Cure SMA has awarded a $50,000 research grant to Rashmi Kothary, PhD, at the University of Ottawa, for his project, ” The shifting landscape of […]
Read More ›Cure SMA Awards $150,000 Grant to Robin Parks, PhD, University of Ottawa
Cure SMA has awarded a $150,000 research grant to Robin Parks, PhD, at the University of Ottawa, for his project, “Serum-derived exosomes as a biomarker […]
Read More ›Cure SMA Awards $75,000 Grant to Robert Kalb, MD, Northwestern University
Cure SMA has awarded a $75,000 research grant to Robert Kalb, MD, at Northwestern University Feinberg School of Medicine, for his project, “Effects of diminished […]
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