New Genentech Data for Evrysdi Show Improved Motor Function in Pre-Symptomatic Babies After One Year and Confirm Safety Profile in Previously Treated People with SMA

1 Comment / Conference, Front Page News, Industry Updates, Research /

Genentech, a member of the Roche Group, today announced new interim data from two studies of Evrysdi® (risdiplam)—JEWELFISH and RAINBOWFISH. Genentech leads the clinical development of Evrysdi as part of a collaboration with the SMA Foundation and PTC Therapeutics. About JEWELFISH Data Data from JEWELFISH, an ongoing open-label study primarily evaluating the safety of Evrysdi in […]

New Genentech Data for Evrysdi Show Improved Motor Function in Pre-Symptomatic Babies After One Year and Confirm Safety Profile in Previously Treated People with SMA Read More »

Biogen Presents New Spinraza Data at the 2021 Virtual SMA Conference

1 Comment / Front Page News, Industry Updates, Research /

Biogen Inc., today announced new research supporting the continued development of an investigational higher dose of SPINRAZA® (nusinersen) and additional data reinforcing the strength of SPINRAZA’s clinical profile in improving the lives of individuals with spinal muscular atrophy (SMA) over the long term. “Intervention with SPINRAZA can meaningfully impact the trajectory of SMA, and we

Biogen Presents New Spinraza Data at the 2021 Virtual SMA Conference Read More »

Community Spotlight: Dr. Arthur Burghes

Leave a Comment / Community Awareness, Community Spotlight, Conference /

On the 25th anniversary of the SMA Researcher Meeting, we would like you to learn more about Dr. Burghes and his commitment to the Cure SMA community. Arthur Burghes, Ph.D., is a Professor of Biological Chemistry and Pharmacology at The Ohio State University and an internationally recognized research scientist who has dedicated more than 30 years

Community Spotlight: Dr. Arthur Burghes Read More »

Ready to Go! Platform Open for 2021 Virtual SMA Conference Events

Leave a Comment / Conference, Front Page News /

Cure SMA is excited to share that the platform for the 2021 Virtual SMA Conference and 2021 Virtual SMA Research & Clinical Care Meeting is officially open! Sessions will kick off tomorrow, Monday, June 7th and run through Friday, June 11th, with a few additional social events trickling into the following week. There is still

Ready to Go! Platform Open for 2021 Virtual SMA Conference Events Read More »

Cure SMA Publishes Manuscript on SMA Awareness, Screening, and Referral Patterns Amongst Pediatricians

Leave a Comment / Front Page News, Our Impact, Research /

In a May 2021 issue of BMC Pediatrics, Cure SMA published a manuscript, titled “Awareness screening and referral patterns among pediatricians in the United States related to early clinical features of spinal muscular atrophy (SMA).” The purpose of the manuscript was to describe the findings of two healthcare provider surveys launched in 2018 and 2019,

Cure SMA Publishes Manuscript on SMA Awareness, Screening, and Referral Patterns Amongst Pediatricians Read More »

Cure SMA Announces 2022 Annual SMA Conference

Leave a Comment / Conference, Front Page News /

Cure SMA is excited to announce that we will reunite the SMA community in-person for the 2022 Annual SMA Conference in Anaheim, CA–Thursday, June 16 through Sunday, June 19, 2022. If the unexpected circumstances surrounding the pandemic have shown us anything, it is how impactful this one week of the year is for individuals, families,

Cure SMA Announces 2022 Annual SMA Conference Read More »

Community Spotlight: Chan Family

Leave a Comment / Community Spotlight, Front Page News /

Ten-year-old Brady Chan from North Carolina has big goals that stem from his passion for video games. He is part of an e-gaming team, where his favorite games include “Brawl Starts” and “Overwatch.” In the future, Brady hopes to become an engineer and create his own video games. He is already learning to code! Brady and his younger brother, Lucas, also love to travel, and Brady hopes to visit France and Japan. “We are always

Community Spotlight: Chan Family Read More »

Cure SMA Launches New Teen & Adult Independence Assistance Package – Check It Out Today!

Leave a Comment / Front Page News, Support & Care /

Along with funding SMA research and care, Cure SMA provides thousands of individuals with SMA and their families with vital support and resources that help them navigate life with SMA. Following a successful 2018 launch of, and sustained interest in, our current Teen & Adult Support Package, Cure SMA is thrilled to offer a supplemental

Cure SMA Launches New Teen & Adult Independence Assistance Package – Check It Out Today! Read More »

Scroll to Top