Research

Cure SMA Awards $140,000 Grant to Joceyln C̫t̩, PhD, University of Ottawa

March 21, 2017
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Cure SMA has awarded a $140,000 research grant to Joceyln Côté, PhD, at The University of Ottawa, for his project, “Investigating the mechanism by which […]

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Cure SMA Awards $140,000 Grant to Arthur Burghes, PhD, The Ohio State University

March 15, 2017
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Cure SMA has awarded a $140,000 research grant to Arthur Burghes, PhD, at The Ohio State University, for his project, “Identification of SMA modifiers and […]

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Biogen Presents New ENDEAR Data Showing SPINRAZA (nusinersen) Significantly Reduces Risk of Death or Permanent Ventilation

January 13, 2017
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Biogen presented new data from the Phase 3 ENDEAR study of SPINRAZA™ (nusinersen), which demonstrated a statistically significant reduction in the risk of death or […]

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Cure SMA Funding Results in 16 New Research Publications

January 4, 2017
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An important goal of our research funding strategy is to share scientific findings with the broader scientific community. To help accomplish this goal, scientists who […]

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2016 Research Year-in-Review: An Historic Year for Our Community

January 4, 2017
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This has been an historic year for the SMA community. On December 23, the FDA announced its approval of Spinraza, the first-ever approved treatment for […]

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The Lancet Publishes Data from Phase 2, Open-Label Trial of Spinraza (Nusinersen) in Infants

December 7, 2016
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Today, Lancet published results from the Phase 2, open-label trial of nusinersen (Spinraza) in infants. This trial initiated in 2013, and patients continue to receive […]

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Cure SMA-Funded Researcher, Chad Heatwole, Publishes Paper on Clinical Trial Outcomes in Adults with SMA

December 5, 2016
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Cure SMA-funded researcher, Chad Heatwole, and his team, have published a paper, “What Matters Most: A Perspective From Adult Spinal Muscular Atrophy Patients”. This project […]

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Over 35 Cure SMA-Funded Researchers Contribute to Comprehensive SMA Encyclopedia

November 22, 2016
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Spinal Muscular Atrophy: Disease Mechanisms and Therapy, the first comprehensive encyclopedia of SMA, has been published by Elsevier. Over thirty five of the book’s authors […]

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Registration is Now Open for the 2017 SMA Researcher Meeting

November 18, 2016
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Registration is now open for industry and academic researchers to attend our 2017 SMA Researcher Meeting, which will be held June 29-July 1 at Disney […]

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Spotlight Innovation Launches Development of STL-182 to Treat SMA

October 31, 2016
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Spotlight Innovation has obtained an exclusive, worldwide license to STL-182, a novel compound invented by Drs. Elliot Androphy at Indiana University and Kevin Hodgetts, director […]

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