Research

Cure SMA-funded Researcher Sara Custer Publishes Paper

October 25, 2016
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Sara Custer, PhD, and her colleagues at Indiana University have published a new paper, “Altered mRNA Splicing in SMN-Depleted Motor Neuron-Like Cells” in the journal […]

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Roche Launches New Phase 2 Clinical Trials

September 23, 2016
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Roche has officially launched two Phase 2 clinical trials testing RO7034067 (also known as RG7916). The trials will begin recruitment in October. Earlier this month, […]

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Catch Up on Research News from the 2016 Family Friendly Research Poster Session

September 19, 2016
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Over the last decade, we’ve seen many advances in spinal muscular atrophy research, from new techniques in gene therapy to drugs that show promise in […]

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Roche Provides New Update on Clinical Development of RG7916

September 16, 2016
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Roche, PTC Therapeutics, and the SMA Foundation have released a community update on the development of their SMN2 splicing modifier clinical development program: Dear SMA […]

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2016 SMA Researcher Meeting Summary: Regulation of SMN Protein Expression and Function

September 14, 2016
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The SMA Researcher Meeting is the largest research meeting in the world specifically focused on SMA. This year we had a record setting 350 attendees. […]

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2016 SMA Researcher Meeting Summary: SMA Therapy Development

September 7, 2016
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The SMA Researcher Meeting is the largest research meeting in the world specifically focused on SMA. This year we had a record setting 350 attendees. […]

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Summer 2016 Issue of Compass Now Available

September 6, 2016
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The Summer 2016 issue of Compass is now available online. As part of our most recent round of funding, we’ve announced $704,000 in funding for […]

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2016 SMA Researcher Meeting Summary: Identification of Candidate Therapeutic Targets and Modifiers, Part 2

September 1, 2016
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The SMA Researcher Meeting is the largest research meeting in the world specifically focused on SMA. This year we had a record setting 350 attendees. […]

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2016 SMA Researcher Meeting Summary: Identification of Candidate Therapeutic Targets and Modifiers, Part 1

August 29, 2016
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The SMA Researcher Meeting is the largest research meeting in the world specifically focused on SMA. This year we had a record setting 350 attendees. […]

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Cure SMA Recognizes Judith Melki on the Anniversary of the Discovery of the SMN Gene

August 25, 2016
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During the 2016 SMA Researcher Meeting, the anniversary of the identification of the SMN genes by Judith Melki MD, PhD (Inserm, Universite Paris) was recognized. […]

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