Research
Ionis Releases Data Update from Phase 2 Study in Infants with SMA
Ionis Pharmaceuticals provided an update on its ongoing open-label Phase 2 clinical study of nusinersen in infants with spinal muscular atrophy (SMA) at the American […]
Read More ›Annual SMA Conference to Host Panels on NDA Process and SMA Drugs in Development
One of the most significant aspects of the Annual SMA Conference is the bringing together of families and researchers in the same event. The 2016 […]
Read More ›Cure SMA-Funded Researchers Receive NIH Grant
Cure SMA-funded researcher Peter Schultz has been awarded a four-year NIH grant of just over $2 million to support his research into small molecules to […]
Read More ›Cure SMA Awards $30,000 Grant to Jocelyn Cote, PhD, University of Ottawa
Cure SMA has awarded a $30,000 research grant to Jocelyn Cote, PhD, at the University of Ottawa for his project, “The role of SMN as […]
Read More ›Cure SMA Awards $140,000 Grant to Arthur Burghes, PhD, The Ohio State University
Cure SMA has awarded a $140,000 research grant to Arthur Burghes, PhD, at The Ohio State University, for his project, “Defining the contribution of RNP […]
Read More ›Cure SMA Awards $90,000 Grant to Antoine Cl̩ry, PhD, ETH Zurich
Cure SMA has awarded a $90,000 research grant to Antoine Cléry, PhD, at ETH Zurich for his project, “Novel approaches against spinal muscular atrophy by […]
Read More ›Cure SMA Awards $140,000 Grant to Christine Beattie, PhD, Ohio State University
Cure SMA has awarded a $140,000 research grant to Christine Beattie, PhD, at the Ohio State University, for her project, “Identification of SMN:HuD bound RNAs […]
Read More ›Record Number of Abstracts Submitted for the 2016 SMA Researcher Meeting
Abstract submission is now closed for the 2016 SMA Researcher Meeting. We are excited to announce that we received 118 submissions, a record number. Our […]
Read More ›Cure SMA-Funded Researchers Publish Paper on Motor Neuron and Astrocyte Defects
Cure SMA-funded researcher Chien-Ping Ko has published a paper in the Journal of Neuroscience, called “Defects in Motoneuron–Astrocyte Interactions in Spinal Muscular Atrophy.” The research […]
Read More ›Patients and Caregivers of Patients with Type II and III SMA Needed for Educational Research Survey
I am a medical education researcher fielding a survey to individuals or caregivers of individuals with Type II or III spinal muscular atrophy (SMA) to […]
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