Research

Cure SMA and PPMD Invite Spinal Muscular Atrophy Parents to Take Part in Two Clinical Trial Surveys

September 12, 2014
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Cure SMA and Parent Project Muscular Dystrophy (PPMD) are conducting two different surveys about clinical trial participation. The goal is to find out more about […]

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Funding Process Reaches Next Steps for Spinal Muscular Atrophy Clinical Care Research

September 11, 2014
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At the end of last week, we announced the close of our for request for proposals (RFP) for clinical care research. A clinical care RFP […]

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Cure SMA Featured in Assay and Drug Development Technologies

September 5, 2014
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Cure SMA was featured in the July/August issue of Assay and Drug Development Technologies, a scientific journal that focuses on the development of new drugs. […]

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Spinal Muscular Atrophy Mice Model Results Published in the Journal Science

August 26, 2014
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On August 7, the journal Science published results of a preclinical study demonstrating that treatment with orally available RNA splicing modifiers of the SMN2 gene […]

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Isis Begins Phase III Clinical Trial

August 25, 2014
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On August 1, Isis Pharmaceuticals, Inc. announced today the initiation of a pivotal Phase III study evaluating ISIS-SMNRx in infants with spinal muscular atrophy (SMA). […]

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Cure SMA Announces New Research Funding

August 25, 2014
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Cure SMA is proud to announce that we will be committing $1.8 million to new research funding over the next 12 months. Fifteen years ago, […]

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