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First ever approved therapy for SMA.

Check out our news section for the latest updates on this important milestone.

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Learn more about the approval of Spinraza.

We recently sat down with SMA researchers, Cure SMA staff, and families in our community to talk about the approval of Spinraza (nusinersen). Listen to their words of gratitude and excitement.

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Spinraza Access Update Webinar

Spinraza Access Update Webinar

On Tuesday, February 14, at 1:00pm EST (10:00am PST/11:00am MST/12:00pm CST), Cure SMA hosted a webinar updating the community on the status of...

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Cure SMA to Host Webinar with the FDA and Patient Advocates

Cure SMA to Host Webinar with the FDA and Patient Advocates

Cure SMA is pleased to announce a new webinar on interactions between the FDA and the SMA community. The webinar will be held on March...

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Cure SMA Launches Newborn Screening Coalition

Cure SMA Launches Newborn Screening Coalition

As SMA drug development continues to move forward, Cure SMA is focused on ensuring that approved therapies are accessible to our entire...

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Cure SMA Launches Community Survey to Address Urgent and Important Issues in SMA Treatment

Cure SMA Launches Community Survey to Address Urgent and Important Issues in SMA Treatment

For the past several years, we've been working to collect data and information on our community's experiences, goals, hopes and challenges....

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Registration Opens for the SMA Patient-Focused Drug Development Meeting with the FDA

Registration Opens for the SMA Patient-Focused Drug Development Meeting with the FDA

Registration is now open for the SMA Patient-Focused Drug Development (PFDD) meeting with the FDA. The PFDD meeting will be held at the College...

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